Department of Biomedical and Molecular Sciences
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Systemic Gene Transfer of a Hexosaminidase Variant Using an scAAV9.47 Vector Corrects GM2 Gangliosidosis in Sandhoff Mice.
Human gene therapy Jul, 2016 | Pubmed ID: 27199088
Queen's University
Karlaina JL Osmon1,
Meera Vyas1,
Evan Woodley2,
Patrick Thompson2,
Jagdeep S Walia1,2,3
1Centre for Neuroscience Studies, Queen's University,
2Department of Biomedical and Molecular Sciences, Queen's University,
3Medical Genetics/ Department of Pediatrics, Kingston General Hospital, Centre for Neuroscience Studies, and Department of Biomedical and Molecular Sciences, Queen's University
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