Punam Malik

Efficient transduction of pigtailed macaque hematopoietic repopulating cells with HIV-based lentiviral vectors.

Placenta growth factor augments endothelin-1 and endothelin-B receptor expression via hypoxia-inducible factor-1 alpha.

Placenta growth factor induces 5-lipoxygenase-activating protein to increase leukotriene formation in sickle cell disease.

Nf1 mutation expands an EGFR-dependent peripheral nerve progenitor that confers neurofibroma tumorigenic potential.

Mechanism of reduction in titers from lentivirus vectors carrying large inserts in the 3'LTR.

A novel human gamma-globin gene vector for genetic correction of sickle cell anemia in a humanized sickle mouse model: critical determinants for successful correction.

Genotoxic potential of lineage-specific lentivirus vectors carrying the beta-globin locus control region.

The 3' region of the chicken hypersensitive site-4 insulator has properties similar to its core and is required for full insulator activity.

Reprogramming erythroid cells for lysosomal enzyme production leads to visceral and CNS cross-correction in mice with Hurler syndrome.

High levels of placenta growth factor in sickle cell disease promote pulmonary hypertension.

Placenta growth factor (PlGF), a novel inducer of plasminogen activator inhibitor-1 (PAI-1) in sickle cell disease (SCD).

Genetic correction of sickle cell anemia and beta-thalassemia: progress and new perspective.

Therapy for beta-globinopathies: a brief review and determinants for successful and safe correction.

Involvement of miR-30c and miR-301a in immediate induction of plasminogen activator inhibitor-1 by placental growth factor in human pulmonary endothelial cells.

Genetic therapy for beta-thalassemia: from the bench to the bedside.

Biomarkers for early detection of sickle nephropathy.

Beyond the definitions of the phenotypic complications of sickle cell disease: an update on management.

Stem cell selection in vivo using foamy vectors cures canine pyruvate kinase deficiency.

G9a/GLP-dependent histone H3K9me2 patterning during human hematopoietic stem cell lineage commitment.

Use of induced pluripotent stem cells to recapitulate pulmonary alveolar proteinosis pathogenesis.

Gene therapy for hemoglobinopathies: the state of the field and the future.

Pulmonary macrophage transplantation therapy.

Peroxisome proliferator-activated receptor-α-mediated transcription of miR-199a2 attenuates endothelin-1 expression via hypoxia-inducible factor-1α.

MicroRNA 648 Targets ET-1 mRNA and is cotranscriptionally regulated with MICAL3 by PAX5.

Perforin gene transfer into hematopoietic stem cells improves immune dysregulation in murine models of perforin deficiency.

Vasculopathy-associated hyperangiotensinemia mobilizes haematopoietic stem cells/progenitors through endothelial AT₂R and cytoskeletal dysregulation.

Erythropoietin-mediated expression of placenta growth factor is regulated via activation of hypoxia-inducible factor-1α and post-transcriptionally by miR-214 in sickle cell disease.

Pigtailed macaques as a model to study long-term safety of lentivirus vector-mediated gene therapy for hemoglobinopathies.

Genetic diminution of circulating prothrombin ameliorates multiorgan pathologies in sickle cell disease mice.

Peroxisome proliferator-activated receptor-α-mediated transcription of miR-301a and miR-454 and their host gene SKA2 regulates endothelin-1 and PAI-1 expression in sickle cell disease.

Placenta growth factor augments airway hyperresponsiveness via leukotrienes and IL-13.

Cardiomyopathy With Restrictive Physiology in Sickle Cell Disease.

Gene Therapy for Hemoglobinopathies: Tremendous Successes and Remaining Caveats.

High Level of Perforin Expression Is Required for Effective Correction of Hemophagocytic Lymphohistiocytosis.

Sickle cell anemia mice develop a unique cardiomyopathy with restrictive physiology.

Activated Transcription Factor 3 in Association with Histone Deacetylase 6 Negatively Regulates MicroRNA 199a2 Transcription by Chromatin Remodeling and Reduces Endothelin-1 Expression.

CRISPR/Cas9 in allergic and immunologic diseases.

The potential of gene therapy approaches for the treatment of hemoglobinopathies: achievements and challenges.

Production and purification of high-titer foamy virus vector for the treatment of leukocyte adhesion deficiency.

Gene therapy for hemoglobin disorders - a mini-review.

Purification of baculovirus vectors using heparin affinity chromatography.

KIT blockade is sufficient for donor hematopoietic stem cell engraftment in Fanconi anemia mice.

A reappraisal of the mechanisms underlying the cardiac complications of sickle cell anemia.

Association between diffuse myocardial fibrosis and diastolic dysfunction in sickle cell anemia.

Losartan for the nephropathy of sickle cell anemia: A phase-2, multicenter trial.

Patient Perspectives on Gene Transfer Therapy for Sickle Cell Disease.

Erratum to: Patient Perspectives on Gene Transfer Therapy for Sickle Cell Disease.

Placenta growth factor mediated gene regulation in sickle cell disease.

Foamy Virus Vector Carries a Strong Insulator in Its Long Terminal Repeat Which Reduces Its Genotoxic Potential.