Iwona Pranke

An unexpected effect of TNF-α on F508del-CFTR maturation and function.

The suppression of premature termination codons and the repair of splicing mutations in CFTR.

Cis variants identified in F508del complex alleles modulate CFTR channel rescue by small molecules.

Factors influencing readthrough therapy for frequent cystic fibrosis premature termination codons.

Might Brushed Nasal Cells Be a Surrogate for CFTR Modulator Clinical Response?

Emerging Therapeutic Approaches for Cystic Fibrosis. From Gene Editing to Personalized Medicine.

Airway surface liquid acidification initiates host defense abnormalities in Cystic Fibrosis.

Cystic Fibrosis Diagnosis in Newborns, Children, and Adults.

Author Correction: Airway surface liquid acidification initiates host defense abnormalities in Cystic Fibrosis.

Urinary Exosomes of Patients with Cystic Fibrosis Unravel CFTR-Related Renal Disease.

Modulators of CFTR. Updates on clinical development and future directions.

New insights into structure and function of bis-phosphinic acid derivatives and implications for CFTR modulation.

Sweat Chloride Testing and Nasal Potential Difference (NPD) Are Primary Outcome Parameters in Treatment with Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) Modulators.

Author Correction: New insights into structure and function of bis-phosphinic acid derivatives and implications for CFTR modulation.

Pharmacological chaperones improve intra-domain stability and inter-domain assembly via distinct binding sites to rescue misfolded CFTR.

Correlating genotype with phenotype using CFTR-mediated whole-cell Cl currents in human nasal epithelial cells.

Systemic bis-phosphinic acid derivative restores chloride transport in Cystic Fibrosis mice.