Measurements of Motor Function and Other Clinical Outcome Parameters in Ambulant Children with Duchenne Muscular DystrophySara Nagy 1,2, Simone Schmidt 1,2, Patricia Hafner 1,3, Andrea Klein 1,4,5, Daniela Rubino-Nacht 1, Vanya Gocheva 1, Oliver Bieri 6, Carole Vuillerot 7, Ulrike Bonati 1,2, Dirk Fischer 1,2,3
1Division of Pediatric Neurology, University Children's Hospital Basel (UKBB), University of Basel, 2Department of Neurology, University Hospital Basel, University of Basel, 3Division of Neurology, University Clinic of Medicine, Cantonal Hospital Baselland, Bruderholz, 4Division of Pediatric Neurology, CHUV, 5Division of Neuropaediatrics, Inselspital, University Children's Hospital Bern, 6Department of Radiology, Division of Radiological Physics, University Hospital Basel, University of Basel, 7Hospices Civils de Lyon, Hôpital Femme-Mère-Enfant, L'Escale, Service de Médecine Physique et de Réadaptation Pédiatrique
The aim of this study is to present the most reliable clinical outcome measures and their correlations with quantitative muscle MRI in ambulant patients with Duchenne muscular dystrophy.