Christina A. Pacak

Genetic fate of recombinant adeno-associated virus vector genomes in muscle.

A targeted gain of function screen in the embryonic CNS of Drosophila.

Recombinant adeno-associated virus serotype 9 leads to preferential cardiac transduction in vivo.

Physiological correction of Pompe disease by systemic delivery of adeno-associated virus serotype 1 vectors.

Long-term skeletal muscle protection after gene transfer in a mouse model of LGMD-2D.

Neonatal intraperitoneal or intravenous injections of recombinant adeno-associated virus type 8 transduce dorsal root ganglia and lower motor neurons.

Tissue specific promoters improve specificity of AAV9 mediated transgene expression following intra-vascular gene delivery in neonatal mice.

Relative persistence of AAV serotype 1 vector genomes in dystrophic muscle.

Injection of isolated mitochondria during early reperfusion for cardioprotection.

Ultrarapid purification of collagen type I for tissue engineering applications.

Pompe disease gene therapy.

AAV vectors for cardiac gene transfer: experimental tools and clinical opportunities.

Transplantation of autologously derived mitochondria protects the heart from ischemia-reperfusion injury.

Microcarrier-based expansion of adult murine side population stem cells.

Biological characterization of F-18-labeled rhodamine B, a potential positron emission tomography perfusion tracer.

Straightening of curved pattern of collagen fibers under load controls aortic valve shape.

Silencing of Drpr Leads to Muscle and Brain Degeneration in Adult Drosophila.